Systematic literature review of the economic burden of spinal muscular atrophy and economic evaluations of treatments

T. Dangouloff, C. Botty, C. Beaudart, L. Servais, M. Hiligsmann

Research output: Contribution to journalReview articleAcademicpeer-review

14 Citations (Web of Science)
Original languageEnglish
Article number47
Number of pages16
JournalOrphanet Journal of Rare Diseases
Volume16
Issue number1
DOIs
Publication statusPublished - 23 Jan 2021

Keywords

  • Burden
  • Cost
  • Cost-effectiveness
  • Economic
  • ICER
  • Nusinersen
  • Onasemnogene abeparvovec
  • Spinal muscular atrophy
  • burden
  • cost
  • cost-effectiveness
  • economic
  • icer
  • nusinersen
  • onasemnogene abeparvovec
  • spinal muscular atrophy
  • COST-EFFECTIVENESS
  • SMA
  • NATURAL-HISTORY
  • NUSINERSEN
  • SHAM CONTROL
  • THERAPY
  • DUCHENNE
  • QUALITY-OF-LIFE

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