OTC intron 4 variations mediate pathogenic splicing patterns caused by the c.386G>A mutation in humans and spf(ash) mice, and govern susceptibility to RNA-based therapies

C. Sacchetto, L. Peretto, F. Baralle, I. Maestri, F. Tassi, F. Bernardi, S.F.J. van de Graaf, F. Pagani, M. Pinotti*, D. Balestra*

*Corresponding author for this work

Research output: Contribution to journalArticleAcademicpeer-review

Fingerprint

Dive into the research topics of 'OTC intron 4 variations mediate pathogenic splicing patterns caused by the c.386G>A mutation in humans and spf(ash) mice, and govern susceptibility to RNA-based therapies'. Together they form a unique fingerprint.

Keyphrases

INIS

Biochemistry, Genetics and Molecular Biology

Immunology and Microbiology