@article{c4583d57f17c425db5ae5f8badf5de5d,
title = "Mitochondrial Neurogastrointestinal Encephalomyopathy Caused by Thymidine Phosphorylase Enzyme Deficiency: From Pathogenesis to Emerging Therapeutic Options",
keywords = "mitochondrial neurogastrointestinal encephalomyopathy, MNGIE, thymidine phosphorylase, metabolic disease, HSCT, HSCGT, lentiviral vector, CELL GENE-THERAPY, CHRONIC GRANULOMATOUS-DISEASE, LONG-TERM SAFETY, LENTIVIRAL VECTOR, MNGIE SYNDROME, DNA DEPLETION, REPLACEMENT THERAPY, HEMATOPOIETIC-CELLS, MURINE MODEL, BONE-MARROW",
author = "Rana Yadak and Smitt, {Peter Sillevis} and {van Gisbergen}, {Marike W.} and {van Til}, {Niek P.} and {de Coo}, {Irenaeus F. M.}",
year = "2017",
month = feb,
day = "15",
doi = "10.3389/fncel.2017.00031",
language = "English",
volume = "11",
journal = "Frontiers in Cellular Neuroscience",
issn = "1662-5102",
publisher = "Frontiers Media S.A.",
}