Is transthyretin amyloid cardiomyopathy heading towards losing its rare disease classification?

Anouk Achten, Steven A Muller, Peter-Paul Zwetsloot, Michelle Michels, Peter van der Meer, Hans L A Nienhuis, Manon G van der Meer, Vanessa P M van Empel, Marish I F J Oerlemans, Christian Knackstedt

Research output: Contribution to journalEditorialAcademicpeer-review

Original languageEnglish
Pages (from-to)1-4
Number of pages4
JournalExpert review of cardiovascular therapy
Volume23
Issue number1-2
DOIs
Publication statusPublished - 10 Feb 2025

Keywords

  • ATTR
  • amyloid
  • amyloidosis
  • cardiomyopathy
  • genetic

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