In vivo proof-of-concept of removal of the huntingtin caspase cleavage motif-encoding exon 12 approach in the YAC128 mouse model of Huntington's disease

Joao Casaca-Carreira, Lodewijk J. A. Toonen, Melvin M. Evers, Ali Jahanshahi, Willeke M. C. van-Roon-Mom, Yasin Temel

Research output: Contribution to journalArticleAcademicpeer-review

Original languageEnglish
Pages (from-to)93-96
JournalBiomedicine & Pharmacotherapy
Volume84
DOIs
Publication statusPublished - Dec 2016

Keywords

  • HD
  • Exon skipping
  • Mouse
  • Intracerebroventricular
  • RNA

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