In utero gene therapy rescues microcephaly caused by Pqbp1-hypofunction in neural stem progenitor cells

H. Ito, H. Shiwaku, C. Yoshida, H. Homma, H. Luo, X. Chen, K. Fujita, L. Musante, U. Fischer, S. G. M. Frints, C. Romano, Y. Ikeuchi, T. Shimamura, S. Imoto, S. Miyano, S-i Muramatsu, T. Kawauchi, M. Hoshino, M. Sudol, A. ArumughanE. E. Wanker, T. Rich, C. Schwartz, F. Matsuzaki, A. Bonni, V. M. Kalscheuer, H. Okazawa

Research output: Contribution to journalArticleAcademicpeer-review

Original languageEnglish
Pages (from-to)459-471
JournalMolecular Psychiatry
Volume20
Issue number4
DOIs
Publication statusPublished - Apr 2015

Cite this

Ito, H., Shiwaku, H., Yoshida, C., Homma, H., Luo, H., Chen, X., Fujita, K., Musante, L., Fischer, U., Frints, S. G. M., Romano, C., Ikeuchi, Y., Shimamura, T., Imoto, S., Miyano, S., Muramatsu, S., Kawauchi, T., Hoshino, M., Sudol, M., ... Okazawa, H. (2015). In utero gene therapy rescues microcephaly caused by Pqbp1-hypofunction in neural stem progenitor cells. Molecular Psychiatry, 20(4), 459-471. https://doi.org/10.1038/mp.2014.69