Building a trusted framework for uncertainty assessment in rare diseases: suggestions for improvement (Response to "TRUST4RD: tool for reducing uncertainties in the evidence generation for specialised treatments for rare diseases")

Sabine E Grimm, Xavier Pouwels, Bram L T Ramaekers, Ben Wijnen, Saskia Knies, Janneke Grutters, Manuela A Joore

Research output: Contribution to journalComment/Letter to the editorAcademicpeer-review

1 Citation (Web of Science)
Original languageEnglish
Article number62
JournalOrphanet Journal of Rare Diseases
Issue number1
Publication statusPublished - 1 Feb 2021


  • Health technology assessment
  • Uncertainty
  • Health economics
  • Orphan diseases

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