A systematic review to evaluate the effectiveness of enzyme replacement therapy for lysosomal storage disorders in comparison to the treatment of similar diseases with higher prevalence

S.H. Lang, N. Armstrong, C. Noake, J. Kleijnen

Research output: Contribution to journalArticleAcademicpeer-review

Original languageEnglish
Pages (from-to)38-56
JournalRare diseases and orphan drugs
Issue number2
Publication statusPublished - 1 Jan 2014

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